Physiological correction of pompe disease by systemic delivery of adeno-associated virus serotype 1 vectors

Cathryn Mah, Christina A. Pacak, Kerry O. Cresawn, Lara R. DeRuisseau, Sean Germain, Melissa A. Lewis, Denise A. Cloutier, David D. Fuller, Barry J. Byrne

Research output: Contribution to journal › Article › peer-review

76 Scopus citations

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Biochemistry, Genetics and Molecular Biology

Keyphrases

Pharmacology, Toxicology and Pharmaceutical Science

Medicine and Dentistry